Ayupova, Aisylu I.; Solovyeva, Valeriya V.; Issa, Shaza S.; Fayoud, Haidar J.; Rizvanov, Albert A. (2025) Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects. International Journal of Molecular Sciences, 26 (20). doi:10.3390/ijms262010107
| Reference Type | Journal (article/letter/editorial) | ||
|---|---|---|---|
| Title | Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects | ||
| Journal | International Journal of Molecular Sciences | ||
| Authors | Ayupova, Aisylu I. | Author | |
| Solovyeva, Valeriya V. | Author | ||
| Issa, Shaza S. | Author | ||
| Fayoud, Haidar J. | Author | ||
| Rizvanov, Albert A. | Author | ||
| Year | 2025 (October 17) | Volume | 26 |
| Issue | 20 | ||
| Publisher | MDPI AG | ||
| DOI | doi:10.3390/ijms262010107Search in ResearchGate | ||
| Generate Citation Formats | |||
| Mindat Ref. ID | 19086587 | Long-form Identifier | mindat:1:5:19086587:2 |
| GUID | 0 | ||
| Full Reference | Ayupova, Aisylu I.; Solovyeva, Valeriya V.; Issa, Shaza S.; Fayoud, Haidar J.; Rizvanov, Albert A. (2025) Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects. International Journal of Molecular Sciences, 26 (20). doi:10.3390/ijms262010107 | ||
| Plain Text | Ayupova, Aisylu I.; Solovyeva, Valeriya V.; Issa, Shaza S.; Fayoud, Haidar J.; Rizvanov, Albert A. (2025) Surrogate Biomarkers in Gene Therapy for Orphan Diseases: Validation, Application, and Regulatory Aspects. International Journal of Molecular Sciences, 26 (20). doi:10.3390/ijms262010107 | ||
| In | (2025, October) International Journal of Molecular Sciences Vol. 26 (20). MDPI AG | ||
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